Healthcare 5 August 2025 - 6 August 2025

The Gene Editing Revolution Transforming Medicine
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How CRISPR Is Curing the Incurable – The Gene Editing Revolution Transforming Medicine

Casgevy became the first CRISPR-based medicine approved for sickle cell disease in the UK and U.S. in late 2023. In June 2025, doctors used a custom CRISPR-Cas system to treat a baby with CPS1 deficiency in Philadelphia. Dozens of CRISPR therapies are in clinical trials worldwide, with Lyfgenia also approved. Doudna and Charpentier won the 2020 Nobel Prize for CRISPR.
August 6, 2025
Gene Therapy
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Gene Therapy Revolution: Cures, Breakthroughs & Challenges in Genetic Medicine

Casgevy became the first FDA-approved CRISPR therapy in December 2023, showing no pain crises in most sickle cell patients during trials. Recent gene therapies include Luxturna, Zolgensma, and Vyjuvek for rare genetic diseases, as well as Hemgenix and Roctavian for hemophilia. CAR-T cell therapies since 2017 have changed blood cancer treatment. Prices for these therapies can reach several million dollars.
August 5, 2025
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